Large genomic mutations within the ATM gene detected by MLPA, including a duplication of 41 kb from exon 4 to 20

Ann Hum Genet. 2008 Jan;72(Pt 1):10-8. doi: 10.1111/j.1469-1809.2007.00399.x. Epub 2007 Oct 3.

Abstract

Mutation detection remains problematic for large genes, primarily because PCR-based methodology fails to detect heterozygous deletions and any duplication. In the ATM gene only a handful of multi-exon deletions have been described to date, and this type of mutation has been considered rare. To address this issue we tested a new MLPA (Multiplex Ligation Probe Amplification) kit that covers 33 of the 66 ATM exons, using for controls two previously characterized genomic deletions in addition to three A-T patients, taken from a survey of nine, who had missing four mutations unidentified after conventional mutation screening. We identified for the first time: 1) a approximately 41 kb genomic duplication spanning exons 4-20 (c.-30_2816dup41kb)(a.k.a., ATM dup 41 kb); 2) a novel genomic deletion including exon 31, and 3) in hemizygosis a point mutation in the non-deleted exon 31. In this study we extended mutation detection to nine new Italian A-T patients, using a combined approach of haplotype analysis, DHPLC and MLPA. Overall we achieved a mutation detection rate of >97%, and can now define a spectrum of ATM mutations based on twenty-one consecutive Italian families with A-T.

Publication types

  • Research Support, N.I.H., Extramural
  • Research Support, Non-U.S. Gov't

MeSH terms

  • Ataxia Telangiectasia Mutated Proteins
  • Case-Control Studies
  • Cell Cycle Proteins / genetics*
  • Chromatography, High Pressure Liquid
  • DNA / genetics
  • DNA / isolation & purification
  • DNA-Binding Proteins / genetics*
  • Exons*
  • Gene Deletion
  • Gene Duplication*
  • Genetic Markers
  • Haplotypes
  • Humans
  • Mutation*
  • Nucleic Acid Amplification Techniques / methods*
  • Pedigree
  • Point Mutation
  • Polymorphism, Single Nucleotide
  • Protein Serine-Threonine Kinases / genetics*
  • Tandem Repeat Sequences
  • Tumor Suppressor Proteins / genetics*

Substances

  • Cell Cycle Proteins
  • DNA-Binding Proteins
  • Genetic Markers
  • Tumor Suppressor Proteins
  • DNA
  • ATM protein, human
  • Ataxia Telangiectasia Mutated Proteins
  • Protein Serine-Threonine Kinases