A novel mutation in a Turkish patient with Hermansky-Pudlak syndrome type 5

Eur J Haematol. 2008 Apr;80(4):356-60. doi: 10.1111/j.1600-0609.2007.01024.x. Epub 2007 Dec 21.

Abstract

The Hermansky-Pudlak syndrome (HPS) is a rare genetically heterogeneous autosomal recessive disorder, characterized by tyrosinase-positive oculocutaneous albinism, platelet dysfunction and lysosomal ceroid lipofuscin storage. This is caused by defects in lysosome-related organelles. In humans eight different types of the syndrome are known, of which a short overview is given. The clinical features and a novel mutation of a patient with HPS type 5 are described here.

Publication types

  • Case Reports
  • Research Support, N.I.H., Intramural

MeSH terms

  • Adult
  • Base Sequence
  • Carrier Proteins / genetics*
  • Female
  • Hermanski-Pudlak Syndrome / classification
  • Hermanski-Pudlak Syndrome / genetics*
  • Humans
  • Mutation / genetics*
  • Turkey

Substances

  • Carrier Proteins
  • HPS5 protein, human