[Restoration of human dystrophin following transplantation of exon-skipping-engineered DMD patient stem cells into dystrophic mice]

Med Sci (Paris). 2008 Jan;24(1):99-101. doi: 10.1051/medsci/200824199.

[Article in French]

Authors

Rachid Benchaouir¹, Mirella Meregalli, Andrea Farini, Giuseppe D'Antona, Marzia Belicchi, Aurélie Goyenvalle, Maurizio Battistelli, Nereo Bresolin, Roberto Bottinelli, Luis Garcia, Yvan Torrente

Affiliation

¹ Stem Cell Laboratory, Department of Neurological Sciences, Fondazione IRCCS Ospedale Maggiore Policlinico, Centro Dino Ferrari, University of Milan, via F. Sforza 35, Milan, Italy.

PMID: 18198122
DOI: 10.1051/medsci/200824199

No abstract available

MeSH terms

Animals
Dystrophin / genetics*
Exons*
Genetic Engineering
Humans
Mice
Muscular Dystrophy, Animal / genetics*
Muscular Dystrophy, Animal / therapy*
Muscular Dystrophy, Duchenne / pathology*
Stem Cell Transplantation*
Transplantation, Heterologous

Substances

Dystrophin