Genetically engineered K cells provide sufficient insulin to correct hyperglycemia in a nude murine model

Acta Biochim Biophys Sin (Shanghai). 2008 Feb;40(2):149-57. doi: 10.1111/j.1745-7270.2008.00387.x.

Abstract

A gene therapy-based treatment of type 1 diabetes mellitus requires the development of a surrogate beta cell that can synthesize and secrete functionally active insulin in response to physiologically relevant changes in ambient glucose levels. In this study, the murine enteroendocrine cell line STC-1 was genetically modified by stable transfection. Two clone cells were selected (STC-1-2 and STC-1-14) that secreted the highest levels of insulin among the 22 clones expressing insulin from 0 to 157.2 microIU/ml/10(6) cells/d. After glucose concentration in the culture medium was increased from 1 mM to 10 mM, secreted insulin rose from 40.3+/-0.8 to 56.3+/-3.2 microIU/ml (STC-1-2), and from 10.8+/-0.8 to 23.6+/-2.3 microIU/ml (STC-1-14). After STC-1-14 cells were implanted into diabetic nude mice, their blood glucose levels were reduced to normal. Body weight loss was also ameliorated. Our data suggested that genetically engineered K cells secrete active insulin in a glucose-regulated manner, and in vivo study showed that hyperglycemia could be reversed by implantation of the cells, suggesting that the use of genetically engineered K cells to express human insulin might provide a glucose-regulated approach to treat diabetic hyperglycemia.

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • Animals
  • Base Sequence
  • Blood Glucose / metabolism
  • Cell Line
  • DNA Primers / genetics
  • Diabetes Mellitus, Experimental / pathology
  • Diabetes Mellitus, Experimental / physiopathology
  • Diabetes Mellitus, Experimental / therapy
  • Diabetes Mellitus, Type 1 / blood
  • Diabetes Mellitus, Type 1 / physiopathology
  • Diabetes Mellitus, Type 1 / therapy
  • Disease Models, Animal
  • Enteroendocrine Cells / metabolism*
  • Enteroendocrine Cells / transplantation*
  • Gene Expression
  • Genetic Engineering
  • Genetic Therapy
  • Glucose Tolerance Test
  • Humans
  • Hyperglycemia / blood
  • Hyperglycemia / physiopathology
  • Hyperglycemia / therapy*
  • Insulin / genetics*
  • Insulin / metabolism*
  • Insulin Secretion
  • Islets of Langerhans / pathology
  • Male
  • Mice
  • Mice, Inbred BALB C
  • Mice, Nude
  • Recombinant Proteins / genetics
  • Recombinant Proteins / metabolism
  • Transfection

Substances

  • Blood Glucose
  • DNA Primers
  • Insulin
  • Recombinant Proteins