Novel method for probing the specificity binding profile of ligands: applications to HIV protease

Chem Biol Drug Des. 2008 May;71(5):387-407. doi: 10.1111/j.1747-0285.2008.00659.x. Epub 2008 Mar 31.

Abstract

A detailed understanding of factors influencing the binding specificity of a ligand to a set of desirable targets and undesirable decoys is a key step in the design of potent and selective therapeutics. We have developed a general method for optimizing binding specificity in ligand-receptor complexes based on the theory of electrostatic charge optimization. This methodology can be used to tune the binding of a ligand to a panel of potential targets and decoys, along the continuum from narrow binding to only one partner to broad binding to the entire panel. Using HIV-1 protease as a model system, we probe specificity in three distinct ways. First, we probe interactions that could make the promiscuous protease inhibitor pepstatin more selective toward HIV-1 protease. Next, we study clinically approved HIV-1 protease inhibitors and probe ways to broaden the binding profiles toward both wild-type HIV-1 protease and drug-resistant mutants. Finally, we study a conformational ensemble of wild-type HIV-1 protease to 'design in' broad specificity to known drugs before resistance mutations arise. The results from this conformational ensemble were similar to those from the drug-resistant ensemble, suggesting the use of a conformational wild-type ensemble as a tool to develop escape-mutant-resistant inhibitors.

Publication types

  • Research Support, N.I.H., Extramural

MeSH terms

  • HIV Protease / chemistry*
  • HIV Protease Inhibitors / chemistry*
  • Ligands
  • Methods
  • Molecular Conformation
  • Protein Binding
  • Static Electricity*
  • Structure-Activity Relationship
  • Substrate Specificity

Substances

  • HIV Protease Inhibitors
  • Ligands
  • HIV Protease