A common Lithuanian mutation causing familial hypercholesterolemia in Ashkenazi Jews

Am J Hum Genet. 1991 Aug;49(2):443-9.

Abstract

Familial hypercholesterolemia (FH) is an autosomal dominant disease caused by mutations in the low-density-lipoprotein (LDL) receptor. Here we characterize an LDL-receptor founder mutation that is associated with a distinct LDL-receptor haplotype and is responsible for FH in 35% of 71 Jewish-Ashkenazi FH families in Israel. Sixty four percent (16/25) of the Ashkenazi patients who carry this mutant allele were of Lithuanian origin. The mutation was not found in 47 non-Ashkenazi FH families. This mutation was prevalent (8/10 FH cases) in the Jewish community in South Africa, which originated mainly from Lithuania. The mutation, a 3-bp in-frame deletion that would result in the elimination of Gly197, has been previously designated FH-Piscataway. PCR amplification of a DNA fragment that includes the mutation in heterozygous individuals results in the formation of a heteroduplex that can be demonstrated by PAGE and used for molecular diagnosis.

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • Alleles
  • Base Sequence
  • DNA / blood
  • DNA / genetics
  • DNA / isolation & purification
  • Ethnicity
  • Female
  • Genes, Dominant
  • Genetic Carrier Screening
  • Haplotypes
  • Humans
  • Hyperlipoproteinemia Type II / blood
  • Hyperlipoproteinemia Type II / genetics*
  • Jews / genetics*
  • Lithuania / ethnology
  • Male
  • Molecular Sequence Data
  • Mutation*
  • Oligonucleotide Probes
  • Polymerase Chain Reaction
  • Receptors, LDL / genetics*
  • Reference Values
  • Restriction Mapping
  • Xanthomatosis / genetics

Substances

  • Oligonucleotide Probes
  • Receptors, LDL
  • DNA