A novel SOX9 mutation, 972delC, causes 46,XY sex-reversed campomelic dysplasia with nephrocalcinosis, urolithiasis, and dysgerminoma

J Pediatr Surg. 2009 Feb;44(2):451-4. doi: 10.1016/j.jpedsurg.2008.10.003.

Abstract

An 8-year-old phenotypic female with campomelic dysplasia (CD) and 46,XY sex-reversal presented with renal colic. Medullary nephrocalcinosis, urolithiasis, and renal malrotation were diagnosed by computed tomographic scanning. Pelvic sonogram identified an enlarged left gonad. Genetic testing revealed a novel SOX9 heterozygous deletion of a cytosine at nucleotide 972 (972delC), causing a frameshift at codon 200, introducing a stop codon 18 codons further downstream (P200fsX218). At laparoscopic gonadectomy, a left dysgerminoma was removed. This first reported case of dysgerminoma in a sex-reversed patient with CD who also had urolithiasis stresses the importance of prophylactic gonadectomy and urologic evaluations in this susceptible population.

Publication types

  • Case Reports

MeSH terms

  • Calcinosis / genetics*
  • Campomelic Dysplasia / genetics*
  • Child
  • Dysgerminoma / genetics*
  • Female
  • Humans
  • Kidney Diseases / genetics*
  • Mutation*
  • Ovarian Neoplasms / genetics*
  • SOX9 Transcription Factor / genetics*
  • Urolithiasis / genetics*

Substances

  • SOX9 Transcription Factor
  • SOX9 protein, human