Abstract
We propose here a general review of current questions related to early trials, including the choice of the primary endpoint, role of bayesian designs, role of stratification and randomization for phase 2 trials, patient selection, and new designs for phase 1 and phase 0 trials. We also discuss the difficulties to apply such methodologies to molecular targeted therapies development.
MeSH terms
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Antineoplastic Agents / therapeutic use
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Bayes Theorem
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Clinical Trials as Topic / methods*
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Clinical Trials as Topic / standards
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Clinical Trials, Phase I as Topic / methods
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Clinical Trials, Phase I as Topic / standards
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Clinical Trials, Phase II as Topic / methods
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Clinical Trials, Phase II as Topic / standards
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Decision Theory
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Drug Screening Assays, Antitumor / methods
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Drug Screening Assays, Antitumor / standards
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Humans
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Neoplasms / therapy*
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Patient Selection
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Randomized Controlled Trials as Topic / methods
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Randomized Controlled Trials as Topic / standards
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Treatment Outcome