A novel mutation of 5alpha-steroid reductase 2 deficiency (CD 65 ALA-PRO) with severe virilization defect in a Turkish family and difficulty in gender assignment

Eur J Pediatr. 2010 Aug;169(8):991-5. doi: 10.1007/s00431-010-1163-1. Epub 2010 Feb 24.

Abstract

Molecular genetic characterization of mutations in SRD5A2 gene is used as an essential procedure for the final diagnosis of 5alpha-reductase deficiency. Here, we report a novel homozygous point mutation of SRD5A2 gene at codon 65 in exon 1, due to a proline for alanine substitution in a Turkish family whose proband has severe undervirilization. This mutation has not been reported up to date in association with 5alpha-reductase deficiency in various ethnic groups. We discussed some questions about gender assignment in addition to the molecular and clinical characteristics of the disease.

Publication types

  • Case Reports

MeSH terms

  • 3-Oxo-5-alpha-Steroid 4-Dehydrogenase / deficiency*
  • 3-Oxo-5-alpha-Steroid 4-Dehydrogenase / genetics*
  • Alanine
  • Child
  • Codon / genetics
  • Exons / genetics
  • Family
  • Female
  • Gender Identity*
  • Homozygote
  • Humans
  • Point Mutation*
  • Proline
  • Sex Characteristics*
  • Turkey

Substances

  • Codon
  • Proline
  • 3-Oxo-5-alpha-Steroid 4-Dehydrogenase
  • Alanine