Alternative pathway or diversion therapy for urea cycle disorders now and in the future

Mol Genet Metab. 2010 Jul;100(3):219-20. doi: 10.1016/j.ymgme.2010.04.008. Epub 2010 Apr 22.

Authors

Stephen Cederbaum¹, Cynthia Lemons, Mark L Batshaw

Affiliation

¹ Department of Psychiatry, Pediatrics and Human Genetics, University of California, Los Angeles (UCLA), Los Angeles, CA, USA.

PMID: 20462778
DOI: 10.1016/j.ymgme.2010.04.008

No abstract available

Publication types

Comment
Historical Article

MeSH terms

Animals
Drug Approval
History, 20th Century
History, 21st Century
Humans
Phenylbutyrates / economics
Phenylbutyrates / history
Phenylbutyrates / therapeutic use
United States
Urea Cycle Disorders, Inborn / drug therapy*
Urea Cycle Disorders, Inborn / economics
Urea Cycle Disorders, Inborn / history

Substances

Phenylbutyrates
4-phenylbutyric acid