The pthaladyns: GTP competitive inhibitors of dynamin I and II GTPase derived from virtual screening

J Med Chem. 2010 Jul 22;53(14):5267-80. doi: 10.1021/jm100442u.

Abstract

We report the development of a homology model for the GTP binding domain of human dynamin I based on the corresponding crystal structure of Dictyostelium discoidum dynamin A. Virtual screening identified 2-[(2-biphenyl-2-yl-1,3-dioxo-2,3-dihydro-1H-isoindole-5-carbonyl)amino]-4-chlorobenzoic acid (1) as a approximately 170 microM potent inhibitor. Homology modeling- and focused library-led synthesis resulted in development of a series of active compounds (the "pthaladyns") with 4-chloro-2-(2-(4-(hydroxymethyl)phenyl)-1,3-dioxoisoindoline-5-carboxamido)benzoic acid (29), a 4.58 +/- 0.06 microM dynamin I GTPase inhibitor. Pthaladyn-29 displays borderline selectivity for dynamin I relative to dynamin II ( approximately 5-10 fold). Only pthaladyn-23 (dynamin I IC(50) 17.4 +/- 5.8 microM) was an effective inhibitor of dynamin I mediated synaptic vesicle endocytosis in brain synaptosomes with an IC(50) of 12.9 +/- 5.9 microM. This compound was also competitive with respect to Mg(2+).GTP. Thus the pthaladyns are the first GTP competitive inhibitors of dynamin I and II GTPase and may be effective new tools for the study of neuronal endocytosis.

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • Benzoates / chemical synthesis*
  • Benzoates / chemistry
  • Benzoates / pharmacology
  • Binding Sites
  • Brain / drug effects
  • Brain / metabolism
  • Dictyostelium
  • Dynamin I / antagonists & inhibitors*
  • Dynamin II / antagonists & inhibitors*
  • Dynamins / chemistry*
  • Endocytosis / drug effects
  • Guanosine Triphosphate / metabolism*
  • Humans
  • Isoindoles / chemical synthesis*
  • Isoindoles / chemistry
  • Isoindoles / pharmacology
  • Kinetics
  • Ligands
  • Models, Molecular
  • Phthalimides / chemical synthesis*
  • Phthalimides / chemistry
  • Phthalimides / pharmacology
  • Protein Conformation
  • Protein Structure, Tertiary
  • Protozoan Proteins / chemistry*
  • Structure-Activity Relationship
  • Synaptosomes / drug effects
  • Synaptosomes / metabolism
  • ortho-Aminobenzoates / chemical synthesis*
  • ortho-Aminobenzoates / chemistry
  • ortho-Aminobenzoates / pharmacology

Substances

  • 4-chloro-2-(2-(4-(hydroxymethyl)phenyl)-1,3-dioxoisoindoline-5-carboxamido)benzoic acid
  • Benzoates
  • Isoindoles
  • Ligands
  • Phthalimides
  • Protozoan Proteins
  • ortho-Aminobenzoates
  • Guanosine Triphosphate
  • Dynamin I
  • Dynamin II
  • Dynamins
  • dynamin A protein, Dictyostelium discoideum