Retrospective analysis of treosulfan-based conditioning in comparison with standard conditioning in patients with myelodysplastic syndrome

Bone Marrow Transplant. 2011 Apr;46(4):502-9. doi: 10.1038/bmt.2010.153. Epub 2010 Jun 28.

Abstract

Myelodysplastic syndromes (MDSs) often occur in older adults with significant comorbidities. Therefore, a reduced-toxicity conditioning regimen may be more suitable than standard conditioning regimens before allogeneic blood stem cell transplantation. Here, we retrospectively compare the outcome of a treosulfan-based conditioning regimen with standard myeloablative TBI-based conditioning regimens in patients (pts) with MDS. A total of 48 pts with MDS were included in the study, of which 29 (60%) pts received TBI-based and 19 (40%) pts received a treosulfan-based conditioning regimen. A significantly lower relapse incidence (5% vs 34% at 3 years, P=0.019) resulting in a better, but not statistically significant relapse-free survival (RFS) (57% vs 31%, P=0.086) was observed after treosulfan-based conditioning. In pts with increased risk for significant side effects due to comorbidities (haematopoietic stem cell transplantation specific comorbidity index), the estimated 3-year RFS was significantly better in the treosulfan group: 54% (95% confidence interval (CI), 17-90%) compared with pts in the TBI group: 11% (95% CI, 0-44%; log-rank test P=0.0455). Treosulfan-based conditioning therapy is a feasible and effective regimen for pts with MDS, especially in pts with preexisting comorbidities.

Publication types

  • Comparative Study

MeSH terms

  • Adolescent
  • Adult
  • Aged
  • Antineoplastic Agents, Alkylating / therapeutic use
  • Busulfan / analogs & derivatives*
  • Busulfan / therapeutic use
  • Comorbidity
  • Disease-Free Survival
  • Humans
  • Middle Aged
  • Myelodysplastic Syndromes / therapy*
  • Recurrence
  • Retrospective Studies
  • Transplantation Conditioning / methods*
  • Treatment Outcome
  • Whole-Body Irradiation
  • Young Adult

Substances

  • Antineoplastic Agents, Alkylating
  • treosulfan
  • Busulfan