Inhibition of Smad3 expression in radiation-induced fibrosis using a novel method for topical transcutaneous gene therapy

Arch Otolaryngol Head Neck Surg. 2010 Jul;136(7):714-9. doi: 10.1001/archoto.2010.107.

Abstract

Objective: To attempt to mitigate the effects of irradiation on murine skin after high-dose radiation using a novel transcutaneous topical delivery system to locally inhibit gene expression with small interfering RNA (siRNA) against Smad3.

Design: Laboratory investigation.

Setting: University laboratory.

Subjects: Twenty-five wild-type C57 mice.

Intervention: In an isolated skin irradiation model, the dorsal skin of C57 wild-type mice was irradiated (45 Gy). Just before irradiation, Smad3 and nonsense siRNA were applied to 2 separate dorsal skin areas and then reapplied weekly. Skin was harvested after 1 and 4 weeks. Smad3 expression were assessed by immunohistochemistry, and collagen deposition and architecture was examined using picrosirius red collagen staining.

Main outcome measures: Epidermal thickness was measured semiquantitatively at 4 weeks. Radiation-induced fibrosis was measured quantitatively via tensiometry. The Young modulus, a measure of cutaneous rigidity inversely related to elasticity, was determined, with normal irradiated skin serving as a control specimen.

Results: Murine skin treated with topical Smad3 siRNA demonstrated effective Smad3 inhibition at 1 week and persistent suppression at 4 weeks. Collagen deposition and epidermal thickness were significantly decreased in skin treated with Smad3 siRNA compared with control irradiated skin. Tensiometry demonstrated decreased tension in Smad3 siRNA-treated skin, with a Young modulus of 9.29 MPa (nonirradiated normal skin, 7.78 MPa) compared with nonsense (control) siRNA-treated skin (14.68 MPa).

Conclusions: Smad3 expression can be effectively silenced in vivo using a novel topical delivery system. Moreover, cutaneous Smad3 inhibition mitigates radiation-induced changes in tissue elasticity, restoring a near-normal phenotype.

Publication types

  • Comparative Study
  • Research Support, Non-U.S. Gov't

MeSH terms

  • Administration, Cutaneous
  • Animals
  • Disease Models, Animal
  • Epidermis / growth & development
  • Epidermis / pathology
  • Fibrosis / pathology
  • Gels
  • Gene Expression Regulation
  • Genetic Therapy / methods*
  • Immunohistochemistry
  • Mice
  • Mice, Inbred C57BL
  • Mice, Knockout
  • RNA, Small Interfering / pharmacology*
  • Radiation Injuries / genetics*
  • Radiation Injuries / pathology
  • Radiation Injuries / therapy*
  • Random Allocation
  • Sensitivity and Specificity
  • Skin / pathology
  • Skin / radiation effects
  • Smad3 Protein / antagonists & inhibitors*
  • Smad3 Protein / genetics
  • Smad3 Protein / metabolism
  • Treatment Outcome
  • Wound Healing / genetics
  • Wound Healing / physiology

Substances

  • Gels
  • RNA, Small Interfering
  • Smad3 Protein