Down-regulation of hepcidin resulting from long-term treatment with an anti-IL-6 receptor antibody (tocilizumab) improves anemia of inflammation in multicentric Castleman disease

Blood. 2010 Nov 4;116(18):3627-34. doi: 10.1182/blood-2010-03-271791. Epub 2010 Jul 19.

Abstract

Dysregulated production of hepcidin is implicated in anemia of inflammation, whereas interleukin-6 (IL-6) is a major inducer of hepcidin production. Overproduction of IL-6 is responsible for pathogenesis of multicentric Castleman disease (MCD), a rare lymphoproliferative disorder accompanied by systemic inflammatory responses and anemia. In this study, we investigated the roles of hepcidin and IL-6 in anemia of inflammation and the long-term effects of anti-IL-6 receptor antibody (tocilizumab) treatment on serum hepcidin and iron-related parameters in MCD patients. We found that tocilizumab treatment resulted in a rapid reduction of serum hepcidin-25 in 5 of 6 MCD patients. Long-term reductions, accompanied by progressive normalization of iron-related parameters and symptom improvement, were observed in 9 of 9 cases 1.5, 3, 6, and 12 months after the start of tocilizumab treatment. In in vitro experiments, IL-6-induced up-regulation of hepcidin mRNA in hepatoma cell lines was completely inhibited by tocilizumab but increased in the presence of patients' sera. Our results suggest that, although multiple factors affect serum hepcidin levels, IL-6 plays an essential role in the induction of hepcidin in MCD. This accounts for the long-term ameliorative effect of IL-6 blockage with tocilizumab on anemia by inhibiting hepcidin production in MCD patients.

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • Anemia / complications
  • Anemia / drug therapy*
  • Anemia / genetics
  • Anemia / immunology
  • Antibodies, Monoclonal / pharmacology
  • Antibodies, Monoclonal / therapeutic use*
  • Antibodies, Monoclonal, Humanized
  • Antimicrobial Cationic Peptides / blood
  • Antimicrobial Cationic Peptides / genetics*
  • Castleman Disease / complications
  • Castleman Disease / drug therapy
  • Castleman Disease / genetics
  • Castleman Disease / immunology
  • Cell Line
  • Down-Regulation / drug effects*
  • Erythropoietin / immunology
  • Hepatocytes / drug effects
  • Hepatocytes / immunology
  • Hepatocytes / metabolism
  • Hepcidins
  • Humans
  • Inflammation / complications
  • Inflammation / drug therapy
  • Inflammation / genetics
  • Inflammation / immunology
  • Interleukin-6 / immunology
  • Iron / metabolism
  • Receptors, Interleukin-6 / immunology*

Substances

  • Antibodies, Monoclonal
  • Antibodies, Monoclonal, Humanized
  • Antimicrobial Cationic Peptides
  • HAMP protein, human
  • Hepcidins
  • Interleukin-6
  • Receptors, Interleukin-6
  • hepcidin 25, human
  • Erythropoietin
  • Iron
  • tocilizumab

Supplementary concepts

  • Multi-centric Castleman's Disease