The molecular basis of α-thalassemia: a model for understanding human molecular genetics

Hematol Oncol Clin North Am. 2010 Dec;24(6):1033-54. doi: 10.1016/j.hoc.2010.08.005. Epub 2010 Sep 29.

Abstract

Down-regulation of α-globin synthesis causes α-thalassemia with underproduction of fetal (HbF, α(2)γ(2)) and adult (HbA, α(2)β(2)) hemoglobin. This article focuses on the human α-globin cluster, which has been characterized in great depth over the past 30 years. In particular the authors describe how the α genes are normally switched on during erythropoiesis and switched off as hematopoietic stem cells commit to nonerythroid lineages. In addition, the principles by which α-globin expression may be perturbed by natural mutations that cause α-thalassemia are reviewed.

Publication types

  • Review

MeSH terms

  • Erythropoiesis / genetics
  • Fetal Hemoglobin / genetics*
  • Hemoglobin A / genetics*
  • Humans
  • Models, Genetic
  • Multigene Family
  • Mutation
  • alpha-Globins / genetics*
  • alpha-Thalassemia / genetics*

Substances

  • alpha-Globins
  • Hemoglobin A
  • Fetal Hemoglobin