Targeting STAT3 in adoptively transferred T cells promotes their in vivo expansion and antitumor effects

Cancer Res. 2010 Dec 1;70(23):9599-610. doi: 10.1158/0008-5472.CAN-10-1293. Epub 2010 Nov 30.

Abstract

Adoptive cell therapy with engineered T cells to improve natural immune response and antitumor functions has shown promise for treating cancer. However, the requirement for extensive ex vivo manipulation of T cells and the immunosuppressive effects of the tumor microenvironment limit this therapeutic modality. In the present study, we investigated the possibility to circumvent these limitations by engineering Stat3 -deficient CD8(+) T cells or by targeting Stat3 in the tumor microenvironment. We show that ablating Stat3in CD8(+) T cells prior to their transfer allows their efficient tumor infiltration and robust proliferation, resulting in increased tumor antigen-specific T-cell activity and tumor growth inhibition. For potential clinical translation, we combined adoptive T-cell therapy with a Food and Drug Administration-approved tyrosine kinase inhibitor, sunitinib, in renal cell carcinoma and melanoma tumor models. Sunitinib inhibited Stat3 in dendritic cells and T cells and reduced conversion of transferred FoxP3(-) T cells to tumor-associated regulatory T cells while increasing transferred CD8(+) T-cell infiltration and activation at the tumor site, leading to inhibition of primary tumor growth. These data show that adoptively transferred T cells can be expanded and activated in vivo either by engineering Stat3-silenced T cells or by targeting Stat3 systemically with small-molecule inhibitors.

Publication types

  • Research Support, N.I.H., Extramural
  • Research Support, Non-U.S. Gov't

MeSH terms

  • Animals
  • Antineoplastic Agents / therapeutic use
  • CD8-Positive T-Lymphocytes / immunology
  • CD8-Positive T-Lymphocytes / metabolism
  • CD8-Positive T-Lymphocytes / transplantation*
  • Cell Line, Tumor
  • Cell Proliferation*
  • Combined Modality Therapy
  • Dendritic Cells / immunology
  • Dendritic Cells / metabolism
  • Female
  • Immunotherapy, Adoptive / methods*
  • Indoles / therapeutic use
  • Lymphocytes, Tumor-Infiltrating / immunology
  • Lymphocytes, Tumor-Infiltrating / metabolism
  • Male
  • Melanoma, Experimental / immunology
  • Melanoma, Experimental / pathology
  • Melanoma, Experimental / therapy*
  • Mice
  • Mice, Inbred BALB C
  • Mice, Inbred C57BL
  • Mice, Knockout
  • Pyrroles / therapeutic use
  • STAT3 Transcription Factor / antagonists & inhibitors
  • STAT3 Transcription Factor / deficiency*
  • STAT3 Transcription Factor / genetics
  • Sunitinib
  • T-Lymphocytes, Regulatory / immunology
  • T-Lymphocytes, Regulatory / metabolism
  • Tumor Burden / drug effects
  • Tumor Burden / immunology

Substances

  • Antineoplastic Agents
  • Indoles
  • Pyrroles
  • STAT3 Transcription Factor
  • Sunitinib