The screening of inborn errors of metabolism in sick Chinese infants by tandem mass spectrometry and gas chromatography/mass spectrometry

Clin Chim Acta. 2011 Jun 11;412(13-14):1270-4. doi: 10.1016/j.cca.2011.03.028. Epub 2011 Apr 2.

Abstract

Background: Analyses of amino acid/acylcarnitines in dried blood spots (DBS) and organic acids in urine are the primary tests for inborn errors of metabolism (IEMs). Automated tandem mass spectrometry (MS/MS) and gas chromatography/mass spectrometry (GC/MS) can rapidly and simultaneously detect numerous metabolic compounds with high precision and sensitivity.

Methods: Three thousand four hundred and twenty-nine DBSs and 2781 urine samples were collected from our hospital patients with suspected IEMs, and analyzed for amino acid/acylcarnitines and organic acids by MS/MS and GC/MS, respectively. The results were used in a coincidental survey to determine the efficacy of these methods for the diagnosis of IEMs.

Results: Nineteen different types of IEMs were detected in 121 affected cases (1.95% of 6210 samples). There were 66.12% amino acid disorders, 29.75% organic acid disorders and 4.13% with fatty acid oxidation disorders.

Conclusions: the sick infants tested in this study had high prevalence rates of neonatal intrahepatic cholestasis, methylmalonic acidemia, hyperphenylalaninemia, tyrosinemia type I, and urea cycle disorders.

Conclusion: The combined use of MS/MS and GC/MS is an appropriate tool for screening of IEMs in sick infants.

MeSH terms

  • Adolescent
  • Amino Acids / blood
  • Asian People*
  • Child
  • Child, Preschool
  • Fatty Acids / metabolism
  • Female
  • Gas Chromatography-Mass Spectrometry / methods*
  • Humans
  • Infant
  • Infant, Newborn
  • Male
  • Metabolism, Inborn Errors / blood
  • Metabolism, Inborn Errors / diagnosis*
  • Metabolism, Inborn Errors / metabolism
  • Metabolism, Inborn Errors / urine
  • Oxidation-Reduction
  • Tandem Mass Spectrometry / methods*

Substances

  • Amino Acids
  • Fatty Acids