Novel missense mutation in the TMPRSS6 gene in a Japanese female with iron-refractory iron deficiency anemia

Int J Hematol. 2011 Jul;94(1):101-103. doi: 10.1007/s12185-011-0881-0. Epub 2011 Jun 4.

Abstract

Iron-refractory iron deficiency anemia (IRIDA) is a rare autosomal-recessive disorder hallmarked by hypochromic microcytic anemia, low transferrin saturation, and unresponsiveness to oral iron with partial recovery after parenteral iron administration. The disease is caused by mutations in TMPRSS6 (transmembrane protease serine 6) that prevent inactivation of membrane-bound hemojuvelin, an activator of hepcidin transcription. To date, 38 cases have been characterized and reported in European countries and the United States. In this paper, we describe the first case of a Japanese female with IRIDA, who carried a novel mutation (K253E) in the CUB (complement factor C1r/C1s, urchin embryonic growth factor and bone morphogenetic protein 1) domain of the TMPRSS6 gene.

Publication types

  • Case Reports

MeSH terms

  • Adult
  • Anemia, Iron-Deficiency / genetics*
  • Asian People
  • Drug Resistance
  • Female
  • Humans
  • Iron / administration & dosage
  • Membrane Proteins / genetics*
  • Mutation, Missense*
  • Rare Diseases*
  • Serine Endopeptidases / genetics*
  • Treatment Outcome

Substances

  • Membrane Proteins
  • Iron
  • Serine Endopeptidases
  • TMPRSS6 protein, human