Pharmacokinetics and pharmacodynamics of a new recombinant FVIII (N8) in haemophilia A mice

Haemophilia. 2012 Jan;18(1):139-45. doi: 10.1111/j.1365-2516.2011.02608.x. Epub 2011 Jul 19.

Abstract

N8 is a new recombinant factor VIII (rFVIII) compound produced and formulated without human- or animal-derived protein. The aims of the present studies were to evaluate the pharmacokinetics and pharmacodynamics properties of N8 and to compare with a commercially available rFVIII product (Advate(®)) in haemophilia A mice. The pharmacokinetics were evaluated after single i.v. administration of 80, 120 and 280 IU kg(-1) of N8 and Advate(®) and measurements of FVIII blood concentrations as a function of time. The efficacy and dose response curves of N8 and Advate(®) (1-200 IU kg(-1)) were evaluated in a tail bleeding model. Furthermore, the effects in a newly developed haemophilia knee joint haemarthrosis model were investigated. No significant differences were found in the pharmacokinetic parameters between N8 and Advate(®). The clearances were 11 ± 1 vs. 10 ± 2 mL h(-1) kg(-1) (P = 0.14) and the half-lives 7.2 ± 0.9 vs. 7.7 ± 1.4 h (P = 0.31) after administration of N8 and Advate(®) respectively. Dose-independent pharmacokinetics was shown, and comparable efficacy and potency were shown between N8 and Advate(®) in the tail bleeding model. Both compounds normalized the bleeding at the dose of 200 IU kg(-1), and for blood loss ED(50) values of 27 IU kg(-1) (N8) and 28 IU/kg (Advate(®)) were found (P = 0.97). In the haemarthrosis model, treatment with N8 and Advate(®) at 200 IU kg(-1) reduced the mean increase in the joint diameter significantly from 1.23 ± 0.19 to 0.32 ± 0.08 mm (P < 0.01) and 0.25 ± 0.08 mm (P < 0.001) respectively. Pharmacokinetics and pharmacodynamics of N8 and Advate(®) were comparable after i.v. administration to haemophilia A mice.

MeSH terms

  • Analysis of Variance
  • Animals
  • Disease Models, Animal
  • Dose-Response Relationship, Drug
  • Factor VIII / pharmacokinetics*
  • Factor VIII / therapeutic use
  • Half-Life
  • Hemarthrosis / drug therapy
  • Hemarthrosis / metabolism
  • Hemophilia A / drug therapy*
  • Hemophilia A / metabolism
  • Hemorrhage / drug therapy
  • Knee Joint
  • Mice
  • Mice, Inbred C57BL
  • Recombinant Proteins / pharmacokinetics
  • Recombinant Proteins / therapeutic use

Substances

  • Recombinant Proteins
  • Factor VIII