The Muenke syndrome mutation (FgfR3P244R) causes cranial base shortening associated with growth plate dysfunction and premature perichondrial ossification in murine basicranial synchondroses

Dev Dyn. 2011 Nov;240(11):2584-96. doi: 10.1002/dvdy.22752.

Abstract

Muenke syndrome caused by the FGFR3(P250R) mutation is an autosomal dominant disorder mostly identified with coronal suture synostosis, but it also presents with other craniofacial phenotypes that include mild to moderate midface hypoplasia. The Muenke syndrome mutation is thought to dysregulate intramembranous ossification at the cranial suture without disturbing endochondral bone formation in the skull. We show in this study that knock-in mice harboring the mutation responsible for the Muenke syndrome (FgfR3(P244R)) display postnatal shortening of the cranial base along with synchondrosis growth plate dysfunction characterized by loss of resting, proliferating and hypertrophic chondrocyte zones and decreased Ihh expression. Furthermore, premature conversion of resting chondrocytes along the perichondrium into prehypertrophic chondrocytes leads to perichondrial bony bridge formation, effectively terminating the postnatal growth of the cranial base. Thus, we conclude that the Muenke syndrome mutation disturbs endochondral and perichondrial ossification in the cranial base, explaining the midface hypoplasia in patients.

Publication types

  • Research Support, N.I.H., Extramural
  • Research Support, Non-U.S. Gov't

MeSH terms

  • Amino Acid Substitution / physiology
  • Animals
  • Arginine / genetics
  • Cranial Sutures / abnormalities
  • Cranial Sutures / diagnostic imaging
  • Cranial Sutures / metabolism
  • Cranial Sutures / pathology
  • Craniosynostoses / genetics*
  • Growth Plate / diagnostic imaging
  • Growth Plate / metabolism
  • Mice
  • Mice, Transgenic
  • Models, Biological
  • Mutation, Missense / physiology
  • Ossification, Heterotopic / genetics*
  • Osteogenesis / genetics
  • Phenotype
  • Proline / genetics
  • Receptor, Fibroblast Growth Factor, Type 3 / genetics*
  • Receptor, Fibroblast Growth Factor, Type 3 / physiology
  • Skull Base / abnormalities*
  • Skull Base / diagnostic imaging
  • Skull Base / metabolism
  • X-Ray Microtomography

Substances

  • Arginine
  • Proline
  • Fgfr3 protein, mouse
  • Receptor, Fibroblast Growth Factor, Type 3

Supplementary concepts

  • Muenke Syndrome