C-terminal tetrapeptides inhibit Aβ42-induced neurotoxicity primarily through specific interaction at the N-terminus of Aβ42

J Med Chem. 2011 Dec 22;54(24):8451-60. doi: 10.1021/jm200982p. Epub 2011 Nov 28.

Abstract

Inhibition of amyloid β-protein (Aβ)-induced toxicity is a promising therapeutic strategy for Alzheimer's disease (AD). Previously, we reported that the C-terminal tetrapeptide Aβ(39-42) is a potent inhibitor of neurotoxicity caused by Aβ42, the form of Aβ most closely associated with AD. Here, initial structure-activity relationship studies identified key structural requirements, including chirality, side-chain structure, and a free N-terminus, which control Aβ(39-42) inhibitory activity. To elucidate the binding site(s) of Aβ(39-42) on Aβ42, we used intrinsic tyrosine (Y) fluorescence and solution-state NMR. The data suggest that Aβ(39-42) binds at several sites, of which the predominant one is located in the N-terminus of Aβ42, in agreement with recent modeling predictions. Thus, despite the small size of Aβ(39-42) and the hydrophobic, aliphatic nature of all four side-chains, the interaction of Aβ(39-42) with Aβ42 is controlled by specific intermolecular contacts requiring a combination of hydrophobic and electrostatic interactions and a particular stereochemistry.

Publication types

  • Research Support, N.I.H., Extramural

MeSH terms

  • Amino Acid Sequence
  • Amyloid beta-Peptides / chemistry*
  • Amyloid beta-Peptides / pharmacology
  • Amyloid beta-Peptides / toxicity
  • Animals
  • Binding Sites
  • Cell Survival / drug effects
  • Fluorescence
  • Hydrophobic and Hydrophilic Interactions
  • Magnetic Resonance Spectroscopy
  • Molecular Sequence Data
  • Neuroprotective Agents / chemistry*
  • Neuroprotective Agents / pharmacology
  • Oligopeptides / chemistry*
  • Oligopeptides / pharmacology
  • PC12 Cells
  • Peptide Fragments / chemistry*
  • Peptide Fragments / pharmacology
  • Peptide Fragments / toxicity
  • Protein Binding
  • Rats
  • Stereoisomerism
  • Structure-Activity Relationship
  • Tyrosine / chemistry

Substances

  • Amyloid beta-Peptides
  • Neuroprotective Agents
  • Oligopeptides
  • Peptide Fragments
  • amyloid beta-peptide (39-42)
  • amyloid beta-protein (1-42)
  • Tyrosine