CDKL5 mutations as a cause of severe epilepsy in infancy: clinical and electroencephalographic long-term course in 4 patients

J Child Neurol. 2013 Jul;28(7):937-41. doi: 10.1177/0883073812451497. Epub 2012 Jul 25.

Abstract

CDKL5 mutations cause severe epilepsy in infancy with subsequent epileptic encephalopathy. As yet, few studies report on long-term observations in patients with CDKL5-related epileptic encephalopathy. In this study, we describe the evolution of the epilepsy phenotype and the electroencephalographic (EEG) features in 4 patients during a maximum observation period of 22 years. All 4 patients had epilepsy starting with focal seizures in the first 3 months of life, evolving to epileptic spasms between the ages of 2 and 6 years and later on to tonic seizures. In 3 patients, epilepsy was resistant to antiepileptic therapy. Although there was no common EEG pattern in all patients, late hypsarrhythmia until the age of 9 years was observed in 2 patients. CDKL5-related epileptic encephalopathies are a group of refractory seizure disorders starting in early infancy. The phenomenon of late hypsarrhythmia may help define a subgroup of patients with severe and adverse outcomes.

Keywords: CDKL5; West syndrome; electroencephalograms; epileptic encephalopathy; late hypsarrhythmia.

MeSH terms

  • Adolescent
  • Age of Onset
  • Anticonvulsants / therapeutic use
  • Brain Waves / drug effects
  • Brain Waves / genetics*
  • Child
  • Child, Preschool
  • Epilepsy / drug therapy
  • Epilepsy / genetics*
  • Epilepsy / physiopathology*
  • Female
  • Humans
  • Longitudinal Studies
  • Male
  • Mutation / genetics*
  • Protein Serine-Threonine Kinases / genetics*
  • Young Adult

Substances

  • Anticonvulsants
  • Protein Serine-Threonine Kinases
  • CDKL5 protein, human