Gene delivery improvement for treating the lysosomal storage disorder metachromatic leukodystrophy
Hum Gene Ther
.
2012 Aug;23(8):793-5.
doi: 10.1089/hum.2012.2516.
Authors
Laura Ferraiuolo
1
,
Brian K Kaspar
Affiliation
1
Center for Gene Therapy, The Research Institute at Nationwide Children's Hospital, Columbus, OH 43205, USA.
PMID:
22900577
DOI:
10.1089/hum.2012.2516
No abstract available
Publication types
Comment
MeSH terms
Animals
Brain / metabolism*
Dependovirus / genetics*
Humans
Leukodystrophy, Metachromatic / genetics*
Leukodystrophy, Metachromatic / therapy*
Oligodendroglia / metabolism*