Gene delivery improvement for treating the lysosomal storage disorder metachromatic leukodystrophy

Hum Gene Ther. 2012 Aug;23(8):793-5. doi: 10.1089/hum.2012.2516.
No abstract available

Publication types

  • Comment

MeSH terms

  • Animals
  • Brain / metabolism*
  • Dependovirus / genetics*
  • Humans
  • Leukodystrophy, Metachromatic / genetics*
  • Leukodystrophy, Metachromatic / therapy*
  • Oligodendroglia / metabolism*