Affinity and cross-reactivity engineering of CTLA4-Ig to modulate T cell costimulation

J Immunol. 2012 Nov 1;189(9):4470-7. doi: 10.4049/jimmunol.1201813. Epub 2012 Sep 26.

Abstract

CTLA4-Ig is an Fc fusion protein containing the extracellular domain of CTLA-4, a receptor known to deliver a negative signal to T cells. CTLA4-Ig modulates T cell costimulatory signals by blocking the CD80 and CD86 ligands from binding to CD28, which delivers a positive T cell costimulatory signal. To engineer CTLA4-Ig variants with altered binding affinity to CD80 and CD86, we employed a high-throughput protein engineering method to map the ligand binding surface of CTLA-4. The resulting mutagenesis map identified positions critical for the recognition of each ligand on the three CDR-like loops of CTLA-4, consistent with the published site-directed mutagenesis and x-ray crystal structures of the CTLA-4/CD80 and CTLA-4/CD86 complexes. A number of single amino acid substitutions were identified that equally affected the binding affinity of CTLA4-Ig for both ligands as well as those that differentially affected binding. All of the high-affinity variants showed improved off-rates, with the best one being a 17.5-fold improved off-rate over parental CTLA4-Ig binding to CD86. Allostimulation of human CD4(+) T cells showed that improvement of CD80 and CD86 binding activity augmented inhibition of naive and primed T cell activation. In general, increased affinity for CD86 resulted in more potent inhibition of T cell response than did increased affinity for CD80. Optimization of the affinity balance to CD80 and CD86 to particular disease settings may lead to development of a CTLA4-Ig molecule with improved efficacy and safety profiles.

MeSH terms

  • Abatacept
  • Animals
  • Arthritis, Rheumatoid / immunology
  • Arthritis, Rheumatoid / pathology
  • Arthritis, Rheumatoid / therapy
  • B7-1 Antigen / antagonists & inhibitors
  • B7-1 Antigen / biosynthesis
  • B7-1 Antigen / genetics
  • B7-2 Antigen / antagonists & inhibitors
  • B7-2 Antigen / biosynthesis
  • B7-2 Antigen / genetics
  • CHO Cells
  • Cricetinae
  • Cricetulus
  • Cross Reactions / genetics
  • Cross Reactions / immunology
  • Genes, Synthetic / immunology
  • HEK293 Cells
  • Humans
  • Immunoconjugates / genetics*
  • Immunoconjugates / metabolism*
  • Immunoconjugates / therapeutic use
  • Jurkat Cells
  • Lymphocyte Activation / genetics*
  • Lymphocyte Activation / immunology*
  • Peptide Library
  • Plasmids / genetics
  • Plasmids / immunology
  • Protein Binding / genetics
  • Protein Binding / immunology
  • T-Lymphocyte Subsets / immunology*
  • T-Lymphocyte Subsets / metabolism*

Substances

  • B7-1 Antigen
  • B7-2 Antigen
  • Immunoconjugates
  • Peptide Library
  • Abatacept