Synthetic silvestrol analogues as potent and selective protein synthesis inhibitors

J Med Chem. 2012 Oct 25;55(20):8859-78. doi: 10.1021/jm3011542. Epub 2012 Oct 12.

Abstract

Misregulation of protein translation plays a critical role in human cancer pathogenesis at many levels. Silvestrol, a cyclopenta[b]benzofuran natural product, blocks translation at the initiation step by interfering with assembly of the eIF4F translation complex. Silvestrol has a complex chemical structure whose functional group requirements have not been systematically investigated. Moreover, silvestrol has limited development potential due to poor druglike properties. Herein, we sought to develop a practical synthesis of key intermediates of silvestrol and explore structure-activity relationships around the C6 position. The ability of silvestrol and analogues to selectively inhibit the translation of proteins with high requirement on the translation-initiation machinery (i.e., complex 5'-untranslated region UTR) relative to simple 5'UTR was determined by a cellular reporter assay. Simplified analogues of silvestrol such as compounds 74 and 76 were shown to have similar cytotoxic potency and better ADME characteristics relative to those of silvestrol.

MeSH terms

  • 5' Untranslated Regions
  • Animals
  • Antineoplastic Agents / chemical synthesis*
  • Antineoplastic Agents / pharmacokinetics
  • Antineoplastic Agents / pharmacology
  • Cell Line, Tumor
  • Drug Screening Assays, Antitumor
  • Genes, Reporter
  • Humans
  • Luciferases / biosynthesis
  • Luciferases / genetics
  • Mice
  • Microsomes, Liver / metabolism
  • Protein Synthesis Inhibitors / chemical synthesis*
  • Protein Synthesis Inhibitors / pharmacokinetics
  • Protein Synthesis Inhibitors / pharmacology
  • Stereoisomerism
  • Structure-Activity Relationship
  • Triterpenes / chemical synthesis*
  • Triterpenes / pharmacokinetics
  • Triterpenes / pharmacology

Substances

  • 5' Untranslated Regions
  • Antineoplastic Agents
  • Protein Synthesis Inhibitors
  • Triterpenes
  • silvestrol
  • Luciferases