BCR-ABL1-induced leukemogenesis and autophagic targeting by arsenic trioxide

Autophagy. 2013 Jan;9(1):93-4. doi: 10.4161/auto.22259. Epub 2012 Oct 10.

Abstract

We have recently shown that arsenic trioxide (As 2O 3) is a potent inducer of autophagic degradation of the BCR-ABL1 oncoprotein, which is the cause of chronic myeloid leukemia (CML) and Ph+ acute lymphoid leukemia (Ph+ ALL). Our recently published work has shown that pharmacological inhibition of autophagy or molecularly targeting of elements of the autophagic machinery partially reverses the suppressive effects of As 2O 3 on primitive leukemic precursors from CML patients. Altogether, our studies have provided direct evidence that arsenic-induced, autophagy-mediated, degradation of BCR-ABL1 is an important mechanism for the generation of the effects of As 2O 3 on BCR-ABL1 transformed leukemic progenitors. These studies raise the potential of future clinical-translational efforts employing combinations of arsenic trioxide with autophagy-modulating agents to promote elimination of early leukemic progenitors and, possibly, leukemia-initiating stem cells.

MeSH terms

  • Antineoplastic Agents / pharmacology
  • Arsenic Trioxide
  • Arsenicals
  • Autophagy / drug effects*
  • Autophagy / physiology
  • Fusion Proteins, bcr-abl / metabolism*
  • Humans
  • Leukemia, Myelogenous, Chronic, BCR-ABL Positive / drug therapy*
  • Leukemia, Myelogenous, Chronic, BCR-ABL Positive / metabolism
  • Leukemia, Myelogenous, Chronic, BCR-ABL Positive / pathology
  • Models, Biological
  • Neoplastic Stem Cells / drug effects
  • Neoplastic Stem Cells / metabolism
  • Neoplastic Stem Cells / pathology
  • Oxides / toxicity*
  • Translational Research, Biomedical

Substances

  • Antineoplastic Agents
  • Arsenicals
  • Oxides
  • Fusion Proteins, bcr-abl
  • Arsenic Trioxide