Identification of novel androgen receptor antagonists using structure- and ligand-based methods

J Chem Inf Model. 2013 Jan 28;53(1):123-30. doi: 10.1021/ci300514v. Epub 2013 Jan 16.

Abstract

Androgen receptor (AR) plays a critical role in the development and progression of prostate cancer (PCa). The AR hormone-binding site (HBS) is intensively studied and represents the target area for current antiandrogens including Bicalutamide and structurally related Enzalutamide. As resistance to antiandrogens invariably emerges in advanced prostate cancer, there exists a high medical need for the identification and development of novel AR antagonists of different chemotypes. Given the wealth of structural information on the AR in complex with a variety of ligands, we have applied an integrated structure- and ligand-based virtual screening methodology to identify novel AR antagonists. Virtual hits generated by a consensus voting approach were experimentally evaluated and resulted in the discovery of a number of structurally diverse submicromolar antagonists of the AR. In particular, one identified compound demonstrated anti-AR potency in vitro that is comparable to the clinically used Bicalutamide. These results set a ground for the development of novel classes of PCa drugs that are structurally different from current AR antagonists.

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • Androgen Receptor Antagonists / chemistry*
  • Androgen Receptor Antagonists / metabolism
  • Androgen Receptor Antagonists / pharmacology*
  • Androgens / metabolism
  • Binding Sites
  • Cell Line, Tumor
  • Cell Proliferation / drug effects
  • Drug Evaluation, Preclinical / methods*
  • Humans
  • Ligands
  • Molecular Docking Simulation
  • Prostate-Specific Antigen / metabolism
  • Quantitative Structure-Activity Relationship
  • Receptors, Androgen / chemistry
  • Receptors, Androgen / metabolism*
  • User-Computer Interface

Substances

  • Androgen Receptor Antagonists
  • Androgens
  • Ligands
  • Receptors, Androgen
  • Prostate-Specific Antigen