Performance evaluation of the next-generation sequencing approach for molecular diagnosis of hereditary hearing loss

Otolaryngol Head Neck Surg. 2013 Jun;148(6):1007-16. doi: 10.1177/0194599813482294. Epub 2013 Mar 22.

Abstract

Objective: To evaluate the performance of a next-generation sequencing (NGS)-based targeted resequencing genetic test, OtoSeq, to identify the sequence variants in the genes causing sensorineural hearing loss (SNHL).

Study design: Retrospective study.

Setting: Tertiary children's hospital.

Subjects and methods: A total of 8 individuals presenting with prelingual hearing loss were used in this study. The coding and flanking intronic regions of 24 well-studied SNHL genes were enriched using microdroplet polymerase chain reaction and sequenced on an Illumina HiSeq 2000 sequencer. The filtered high-quality sequence reads were mapped to reference sequence, and variants were detected using NextGENe software.

Results: A total of 1148 sequence variants were detected in 8 samples in 24 genes. Using in-house developed NGS data analysis criteria, we classified 810 (~71%) of these variants as potential true variants that include previously detected pathogenic mutations in 5 patients. To validate our strategy, we Sanger sequenced the target regions of 5 of the 24 genes, accounting for about 29.2% of all target sequence. Our results showed >99.99% concordance between NGS and Sanger sequencing in these 5 genes, resulting in an analytical sensitivity and specificity of 100% and 99.997%, respectively. We were able to successfully detect single base substitutions, small deletions, and insertions of up to 22 nucleotides.

Conclusion: This study demonstrated that our NGS-based mutation screening strategy is highly sensitive and specific in detecting sequence variants in the SNHL genes. Therefore, we propose that this NGS-based targeted sequencing method would be an alternative to current technologies for identifying the multiple genetic causes of SNHL.

Keywords: clinical diagnosis; genetic etiology; hearing loss; microdroplet PCR; mutation screening; next-generation sequencing.

Publication types

  • Comparative Study
  • Evaluation Study
  • Research Support, Non-U.S. Gov't

MeSH terms

  • Adolescent
  • Age Factors
  • Child
  • Child, Preschool
  • Cohort Studies
  • Female
  • Follow-Up Studies
  • Genetic Predisposition to Disease*
  • Genetic Testing / methods
  • Hearing Loss, Sensorineural / diagnosis
  • Hearing Loss, Sensorineural / epidemiology
  • Hearing Loss, Sensorineural / genetics*
  • High-Throughput Nucleotide Sequencing / methods*
  • Hospitals, Pediatric
  • Humans
  • Incidence
  • Infant
  • Male
  • Polymerase Chain Reaction / methods
  • Retrospective Studies
  • Risk Assessment
  • Sensitivity and Specificity
  • Sequence Analysis, DNA / methods*
  • Sex Factors
  • United States