Wolfram gene (WFS1) mutation causes autosomal dominant congenital nuclear cataract in humans

Eur J Hum Genet. 2013 Dec;21(12):1356-60. doi: 10.1038/ejhg.2013.52. Epub 2013 Mar 27.

Abstract

Congenital cataracts are an important cause of bilateral visual impairment in infants. Through genome-wide linkage analysis in a four-generation family of Irish descent, the disease-associated gene causing autosomal-dominant congenital nuclear cataract was mapped to chromosome 4p16.1. The maximum logarithm of odds (LOD) score was 2.62 at a recombination fraction θ=0, obtained for marker D4S432 physically close to the Wolfram gene (WFS1). By sequencing the coding regions and intron-exon boundaries of WFS1, we identified a DNA substitution (c.1385A-to-G) in exon 8, causing a missense mutation at codon 462 (E462G) of the Wolframin protein. This is the first report of a mutation in this gene causing an isolated nuclear congenital cataract. These findings suggest that the membrane trafficking protein Wolframin may be important for supporting the developing lens.

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • Base Sequence
  • Cataract / congenital*
  • Cataract / genetics
  • Exons / genetics
  • Female
  • Genes, Dominant / genetics*
  • Genetic Linkage / genetics
  • Genetic Predisposition to Disease / genetics*
  • Genotype
  • Humans
  • Introns / genetics
  • Male
  • Membrane Proteins / genetics*
  • Molecular Sequence Data
  • Mutation, Missense / genetics*
  • Pedigree
  • Polymorphism, Single Nucleotide / genetics

Substances

  • Membrane Proteins
  • wolframin protein

Supplementary concepts

  • Cataract, Autosomal Dominant Nuclear