Cutaneous toxicities of BRAF inhibitors: clinical and pathological challenges and call to action

Crit Rev Oncol Hematol. 2013 Nov;88(2):318-37. doi: 10.1016/j.critrevonc.2013.06.002. Epub 2013 Jul 3.

Abstract

Somatic mutations in the BRAF gene have been identified as the most frequent and relevant to develop targeted molecular therapies in melanoma. Recently, seminal clinical trials have provided indisputable evidence that BRAF inhibitors improve response rate, progression free and overall survival in BRAFV600 mutated metastatic melanoma patients, thus representing the novel standard of care. Dermatological "off target" effects of these so-called 'targeted therapies' have to be considered, however, and among them the most intriguing are cutaneous adverse reactions. Skin toxicity is of relevance for at least three reasons: (1) it worsens the patient's quality of life and may be difficult to manage, (2) its heterogeneous clinical presentation differs from the clinico-pathological pictures observed in patients who do not receive BRAF inhibitors, and; (3) onset of skin cancer represents a model of carcinogenesis which may help to better understand the potential visceral tumorigenesis induced by BRAF inhibitors. This manuscript summarizes and critically reviews the state of the art of skin toxicity associated with BRAF inhibitors. Special attention will be paid to clinical presentation and histopathological findings, as well as related challenges for clinicians, pathologists, and basic scientists.

Keywords: BRAF inhibitors; Clinical; Histopathology; Management; Melanoma; Skin toxicity.

Publication types

  • Research Support, Non-U.S. Gov't
  • Review

MeSH terms

  • Antineoplastic Agents / adverse effects*
  • Antineoplastic Agents / therapeutic use
  • Carcinoma, Squamous Cell / chemically induced
  • Carcinoma, Squamous Cell / diagnosis
  • Humans
  • Melanoma / complications*
  • Melanoma / drug therapy
  • Protein Kinase Inhibitors / adverse effects*
  • Protein Kinase Inhibitors / therapeutic use
  • Proto-Oncogene Proteins B-raf / antagonists & inhibitors
  • Research
  • Skin / drug effects
  • Skin / pathology
  • Skin Diseases / chemically induced*
  • Skin Diseases / diagnosis
  • Skin Diseases / therapy

Substances

  • Antineoplastic Agents
  • Protein Kinase Inhibitors
  • Proto-Oncogene Proteins B-raf