Pharmacologic inhibition of PKCα and PKCθ prevents GVHD while preserving GVL activity in mice

Blood. 2013 Oct 3;122(14):2500-11. doi: 10.1182/blood-2012-12-471938. Epub 2013 Aug 1.

Abstract

Allogeneic hematopoietic cell transplantation (HCT) is the most effective therapy for hematopoietic malignancies through T-cell-mediated graft-vs-leukemia (GVL) effects but often leads to severe graft-vs-host disease (GVHD). Given that protein kinase Cθ (PKCθ), in cooperation with PKCα, is essential for T-cell signaling and function, we have evaluated PKCθ and PKCα as potential therapeutic targets in allogeneic HCT using genetic and pharmacologic approaches. We found that the ability of PKCα(-/-)/θ(-/-) donor T cells to induce GVHD was further reduced compared with PKCθ(-/-) T cells in relation with the relevance of both isoforms to allogeneic donor T-cell proliferation, cytokine production, and migration to GVHD target organs. Treatment with a specific inhibitor for both PKCθ and PKCα impaired donor T-cell proliferation, migration, and chemokine/cytokine production and significantly decreased GVHD in myeloablative preclinical murine models of allogeneic HCT. Moreover, pharmacologic inhibition of PKCθ and PKCα spared T-cell cytotoxic function and GVL effects. Our findings indicate that PKCα and θ contribute to T-cell activation with overlapping functions essential for GVHD induction while less critical to the GVL effect. Thus, targeting PKCα and PKCθ signaling with pharmacologic inhibitors presents a therapeutic option for GVHD prevention while largely preserving the GVL activity in patients receiving HCT.

Publication types

  • Research Support, N.I.H., Extramural

MeSH terms

  • Animals
  • Cell Separation
  • Disease Models, Animal
  • Enzyme Inhibitors / pharmacology
  • Flow Cytometry
  • Graft vs Host Disease / enzymology
  • Graft vs Host Disease / prevention & control*
  • Graft vs Leukemia Effect / drug effects*
  • Hematopoietic Stem Cell Transplantation / adverse effects
  • Isoenzymes / antagonists & inhibitors*
  • Leukemia / therapy
  • Lymphocyte Activation / drug effects
  • Lymphoma / therapy
  • Mice
  • Mice, Inbred BALB C
  • Mice, Inbred C57BL
  • Mice, Knockout
  • Protein Kinase C / antagonists & inhibitors*
  • Protein Kinase C-alpha / antagonists & inhibitors*
  • Protein Kinase C-theta
  • T-Lymphocytes / drug effects
  • T-Lymphocytes / immunology

Substances

  • Enzyme Inhibitors
  • Isoenzymes
  • Prkcq protein, mouse
  • Protein Kinase C
  • Protein Kinase C-alpha
  • Protein Kinase C-theta