MicroRNA-based strategy to mitigate the risk of gain-of-function influenza studies

Nat Biotechnol. 2013 Sep;31(9):844-847. doi: 10.1038/nbt.2666. Epub 2013 Aug 11.

Abstract

Recent gain-of-function studies in influenza A virus H5N1 strains revealed that as few as three-amino-acid changes in the hemagglutinin protein confer the capacity for viral transmission between ferrets. As transmission between ferrets is considered a surrogate indicator of transmissibility between humans, these studies raised concerns about the risks of gain-of-function influenza A virus research. Here we present an approach to strengthen the biosafety of gain-of-function influenza experiments. We exploit species-specific endogenous small RNAs to restrict influenza A virus tropism. In particular, we found that the microRNA miR-192 was expressed in primary human respiratory tract epithelial cells as well as in mouse lungs but absent from the ferret respiratory tract. Incorporation of miR-192 target sites into influenza A virus did not prevent influenza replication and transmissibility in ferrets, but did attenuate influenza pathogenicity in mice. This molecular biocontainment approach should be applicable beyond influenza A virus to minimize the risk of experiments involving other pathogenic viruses.

Publication types

  • Research Support, N.I.H., Extramural
  • Research Support, Non-U.S. Gov't
  • Research Support, U.S. Gov't, Non-P.H.S.

MeSH terms

  • Animals
  • Biomedical Research* / methods
  • Biomedical Research* / standards
  • Body Weight
  • Ferrets
  • Humans
  • Influenza A Virus, H5N1 Subtype* / genetics
  • Influenza A Virus, H5N1 Subtype* / pathogenicity
  • Mice
  • MicroRNAs* / genetics
  • MicroRNAs* / metabolism
  • Orthomyxoviridae Infections / virology
  • Risk Management
  • Survival Analysis
  • Viral Tropism / genetics
  • Virology* / methods
  • Virology* / standards
  • Virus Replication / genetics

Substances

  • MicroRNAs