Beriate® P in the treatment of patients with haemophilia A: results of a long-term pharmacovigilance study

Thromb Res. 2014 Nov:134 Suppl 1:S16-21. doi: 10.1016/j.thromres.2013.10.014. Epub 2014 Jan 10.

Abstract

Background: The German Beriate(®) P pharmacovigilance study started in 2003 and is planned to run until December 2013.

Materials and methods: This analysis included data from 84 haemophilia A patients treated with the high-purity, plasma-derived coagulation factor VIII concentrate Beriate(®) P. Prior to study start, 69 of the 80 patients for whom data were available had received previous treatment with Beriate(®) P (mean treatment period 7.1 ± 5.4 years). The mean study duration from the start of pharmacovigilance was 43.3 ± 30.3 months (median 43.5 months; range 0-101.9months). The most common treatment at the last visit was prophylaxis (65.7% of patients), which was most commonly administered at a frequency of three infusions/week in 47.3% of patients.

Results: Most patients experienced up to six minor bleeds/year. For 1,311 bleeding episodes, a median of one infusion/bleed was administered (mean 2.8 ± 4.7; range 0-83). The clinical response to Beriate(®) P was rated "excellent"/"good" in 94% of 32 visits of patients with major bleeding. The clinical response for patients with minor bleeding was rated "excellent"/"good" in 98.5% of 377 visits. One clinically relevant inhibitor in a previously untreated patient was documented during the study course. There were no reports of virus transmissions suspected to be caused by Beriate(®) P prior to the study start or during the study.

Conclusions: These findings confirm the excellent efficacy, safety, and tolerability of Beriate(®) P in the treatment of a wide spectrum of previously untreated patients up to adult patients with haemophilia A.

Keywords: Beriate(®) P; Efficacy; Haemophilia A; Inhibitors; Pharmacovigilance; Safety.

Publication types

  • Multicenter Study
  • Observational Study
  • Research Support, Non-U.S. Gov't

MeSH terms

  • Adolescent
  • Adult
  • Aged
  • Child
  • Child, Preschool
  • Drug Combinations
  • Factor VIII / administration & dosage
  • Factor VIII / adverse effects
  • Factor VIII / economics
  • Factor VIII / therapeutic use*
  • Female
  • Hemophilia A / complications
  • Hemophilia A / drug therapy*
  • Hemophilia A / economics
  • Hemorrhage / complications
  • Humans
  • Infant
  • Male
  • Middle Aged
  • Plasma / virology
  • Prospective Studies
  • Young Adult
  • von Willebrand Factor / administration & dosage
  • von Willebrand Factor / adverse effects
  • von Willebrand Factor / economics
  • von Willebrand Factor / therapeutic use*

Substances

  • Drug Combinations
  • factor VIII, von Willebrand factor drug combination
  • von Willebrand Factor
  • Factor VIII