Apoptosis therapy in cancer: the first single-molecule co-activating p53 and the translocator protein in glioblastoma

Sci Rep. 2014 Apr 23:4:4749. doi: 10.1038/srep04749.

Abstract

In the complex scenario of cancer, treatment with compounds targeting multiple cell pathways has been emerging. In Glioblastoma Multiforme (GBM), p53 and Translocator Protein (TSPO), both acting as apoptosis inducers, represent two attractive intracellular targets. On this basis, novel indolylglyoxylyldipeptides, rationally designed to activate TSPO and p53, were synthesized and biologically characterized. The new compounds were able to bind TSPO and to reactivate p53 functionality, through the dissociation from its physiological inhibitor, murine double minute 2 (MDM2). In GBM cells, the new molecules caused Δψm dissipation and inhibition of cell viability. These effects resulted significantly higher with respect to those elicited by the single target reference standards applied alone, and coherent with the synergism resulting from the simultaneous activation of TSPO and p53. Taken together, these results suggest that TSPO/MDM2 dual-target ligands could represent a new attractive multi-modal opportunity for anti-cancer strategy in GBM.

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • Animals
  • Antineoplastic Agents / chemistry
  • Antineoplastic Agents / pharmacology*
  • Apoptosis / drug effects*
  • Binding Sites
  • Cell Cycle / drug effects
  • Cell Line, Tumor
  • Cell Survival / drug effects
  • Glioblastoma / drug therapy
  • Glioblastoma / metabolism*
  • Humans
  • Membrane Potential, Mitochondrial
  • Mice
  • Models, Molecular
  • Molecular Conformation
  • Nuclear Magnetic Resonance, Biomolecular
  • Protein Binding
  • Protein Interaction Mapping
  • Proto-Oncogene Proteins c-mdm2 / chemistry
  • Proto-Oncogene Proteins c-mdm2 / metabolism
  • Receptors, GABA / chemistry
  • Receptors, GABA / metabolism*
  • Tumor Suppressor Protein p53 / agonists*
  • Tumor Suppressor Protein p53 / chemistry

Substances

  • Antineoplastic Agents
  • Receptors, GABA
  • TSPO protein, human
  • Tumor Suppressor Protein p53
  • Proto-Oncogene Proteins c-mdm2