Allogeneic hematopoietic cell transplantation without total body irradiation from unrelated donor in adult patients with idiopathic aplastic anemia: fludarabine versus cyclophosphamide-ATG

Leuk Res. 2014 Jul;38(7):730-6. doi: 10.1016/j.leukres.2014.01.002. Epub 2014 Jan 10.

Abstract

Total body irradiation (TBI) has traditionally been used in the conditioning regimen for allogenetic hematopoietic stem cell transplantation (alloHCT) from an unrelated donor (u-HCT). However, patients are increasingly receiving a fludarabine-based conditioning regimen without TBI, as it seemed less toxic than TBI. We need to know the clinical results of non-TBI u-HCT treatments. We retrospectively investigated the clinical outcomes of allogenetic hematopoietic cell transplantation (alloHCT) from an unrelated donor without TBI (non-TBI u-HCT) and compared the clinical outcomes of fludarabine-based (FLU group) and cyclophosphamide-ATG (Cy-ATG group) conditioning regimens. Sixty-one patients received the non-TBI conditioning regimen for u-HCT (32 in the FLU group and 29 in the Cy-ATG group). The cumulative incidence of neutrophil engraftment at 30 days, platelet>20K/μL at 30 days, acute graft-versus host disease (aGvHD) at 100 days, and chronic GvHD (cGvHD) at 2 years were 87.01%, 65.57%, 35.20%, and 26.64%, respectively. However, transplantation outcomes and overall survival rates did not differ between the FLU and Cy-ATG groups. Only infused CD34+ cells >3×10(6)kg(-1) was identified as a favorable factor for survival in the multivariate analysis. In conclusion, non-TBI u-HCT was feasible and there was no difference between the FLU and Cy-ATG groups in terms of transplantation outcomes.

Keywords: Allogeneic hematopoietic stem cell transplantation; Aplastic anemia; Fludarabine; Total body irradiation; Unrelated donor.

Publication types

  • Comparative Study
  • Research Support, Non-U.S. Gov't

MeSH terms

  • Adolescent
  • Adult
  • Anemia, Aplastic / mortality
  • Anemia, Aplastic / therapy*
  • Antilymphocyte Serum / administration & dosage*
  • Child
  • Cyclophosphamide / administration & dosage*
  • Female
  • Hematopoietic Stem Cell Transplantation* / mortality
  • Histocompatibility Testing
  • Humans
  • Male
  • Middle Aged
  • Prognosis
  • Retrospective Studies
  • Transplantation Conditioning*
  • Transplantation, Homologous
  • Vidarabine / analogs & derivatives*
  • Vidarabine / therapeutic use
  • Whole-Body Irradiation

Substances

  • Antilymphocyte Serum
  • Cyclophosphamide
  • Vidarabine
  • fludarabine

Supplementary concepts

  • Aplastic anemia, idiopathic