Phenotypic variability in congenital lipoid adrenal hyperplasia

Indian Pediatr. 2014 May;51(5):399-400.

Abstract

Background: Congenital lipoid adrenal hyperplasia presents with adrenal insufficiency and sex reversal in 46XY genetic males.

Case characteristics: Two patients (46 XY karyotype), one having ambiguous genitalia and other having female external genitalia, presented with adrenal crisis at 6 months and 4 weeks of age, respectively.

Observation: Steroidogenic Acute Regulatory Protein gene sequencing revealed homozygous mutations in both patients.

Outcome: Treatment with hydrocortisone and fludrocortisone resulted in marked improvement.

Message: Congenital lipoid adrenal hyperplasia should be considered in infants having female or ambiguous genitalia, and presenting with adrenal insufficiency.

Publication types

  • Case Reports

MeSH terms

  • Adrenal Hyperplasia, Congenital*
  • Disorder of Sex Development, 46,XY*
  • Female
  • Humans
  • Infant
  • Male
  • Phenotype
  • Phosphoproteins / genetics
  • Steroidogenic Acute Regulatory Protein

Substances

  • Phosphoproteins
  • Steroidogenic Acute Regulatory Protein

Supplementary concepts

  • Lipoid congenital adrenal hyperplasia