[Thalidomide teratogenicity and its direct target identification]

Nihon Rinsho. 2015 Jan;73(1):143-8.
[Article in Japanese]

Abstract

Half a century ago, thalidomide was developed as a sedative drug and was wildly used over 40 countries. However the drug has serious birth defects such as amelia and phocomelia. Now thalidomide is regarded as a clinically effective drug and used for the treatment of multiple myeloma under strict controls. The direct target of thalidomide had been a long-standing question. We identified cereblon as a primary direct target protein for thalidomide teratogenicity using new affinity bead technology in 2010. In this review, we introduce an overview of thalidomide teratogenicity, a story about how we identified cereblon, and recent advances in cereblon studies.

Publication types

  • Review

MeSH terms

  • Adaptor Proteins, Signal Transducing
  • Animals
  • Humans
  • Molecular Targeted Therapy
  • Multiple Myeloma / drug therapy*
  • Peptide Hydrolases / metabolism
  • Teratogenesis*
  • Thalidomide / adverse effects
  • Thalidomide / chemistry
  • Thalidomide / therapeutic use*
  • Ubiquitin-Protein Ligases

Substances

  • Adaptor Proteins, Signal Transducing
  • CRBN protein, human
  • Thalidomide
  • Ubiquitin-Protein Ligases
  • Peptide Hydrolases