Harnessing RNA interference for therapy: the silent treatment

JAMA. 2015 Mar;313(12):1207-8. doi: 10.1001/jama.2015.1241.

Authors

Judy Lieberman¹, Phillip A Sharp²

Affiliations

¹ Program in Cellular and Molecular Medicine, Boston Children's Hospital, Boston, Massachusetts2Department of Pediatrics, Harvard Medical School, Boston, Massachusetts.
² Koch Institute for Integrative Cancer Research, Massachusetts Institute of Technology, Cambridge, Massachusetts.

PMID: 25803342
DOI: 10.1001/jama.2015.1241

No abstract available

MeSH terms

Gene Knockdown Techniques
Genetic Therapy / methods*
Hemophilia A / therapy
Humans
Liver / drug effects
RNA Interference*
RNA, Small Interfering

Substances

RNA, Small Interfering