Identification of anti-thrombopoietin receptor antibody in prolonged thrombocytopenia after allogeneic hematopoietic stem cell transplantation treated successfully with eltrombopag

Int J Hematol. 2015 Oct;102(4):471-6. doi: 10.1007/s12185-015-1806-0. Epub 2015 May 13.

Abstract

A 55-year-old female with stage IVA follicular lymphoma in third complete remission underwent allogeneic peripheral blood stem cell transplantation. Neutrophil engraftment was achieved on day +18; however, platelet counts remained below 10 × 10(3)/µL, necessitating transfusions twice a week for more than 3 months. Bone marrow showed a decreased number of megakaryocytes with hypolobulated nuclei. No graft versus host disease, viral infection, or disease relapse was observed. Furthermore, severe thrombocytopenia below 5.0 × 10(3)/µL refractory to transfusion appeared on day +240 after influenza virus infection. Treatments with intravenous immunoglobulin, romiplostim, and rituximab were administered without any recovery. Subsequently, eltrombopag was initiated on day +443, after which platelet counts rose gradually and continued to rise above 20 × 10(3)/µL after 10 weeks of administration. The serum thrombopoietin (TPO) level was markedly elevated, and anti-TPO receptor (TPOR) antibody was detected in the patient's serum. Anti-TPOR antibody may play an important role in some cases of prolonged thrombocytopenia after allogeneic hematopoietic stem cell transplantation with unknown etiology, and eltrombopag could be a novel therapeutic option for such cases.

Keywords: Allogeneic hematopoietic stem cell transplantation; Anti-thrombopoietin receptor antibody; Eltrombopag; Prolonged thrombocytopenia.

Publication types

  • Case Reports

MeSH terms

  • Allografts
  • Autoantibodies / blood*
  • Benzoates / administration & dosage*
  • Female
  • Hematopoietic Stem Cell Transplantation*
  • Humans
  • Hydrazines / administration & dosage*
  • Lymphoma, Follicular* / blood
  • Lymphoma, Follicular* / therapy
  • Middle Aged
  • Pyrazoles / administration & dosage*
  • Receptors, Thrombopoietin*
  • Thrombocytopenia* / blood
  • Thrombocytopenia* / drug therapy

Substances

  • Autoantibodies
  • Benzoates
  • Hydrazines
  • Pyrazoles
  • Receptors, Thrombopoietin
  • MPL protein, human
  • eltrombopag