Rib and vertebral bone fibrous dysplasia in a child with tuberous sclerosis complex

Am J Med Genet A. 2015 Nov;167A(11):2755-7. doi: 10.1002/ajmg.a.37235. Epub 2015 Jul 14.

Abstract

Tuberous sclerosis complex (TSC) is an autosomal dominant genetic disorder characterized by benign hamartomas in multiple organ systems, primarily the skin, brain, heart, kidneys, lungs, and eyes. The skeletal system is commonly affected in patients with TSC, but these bone lesions are generally asymptomatic and have not been well characterized. We present clinically significant bone growth in two ribs and vertebrae in an 8-year-old male patient with TSC and discuss the effects of mammalian target of rapamycin (mTOR) inhibitors as a possible treatment for these osseous abnormalities. This report suggests that skeletal lesions may hold more clinical significance than previously assumed and that further research should be directed toward understanding bone involvement in TSC.

Keywords: bone lesion; fibrous dysplasia; mTOR inhibitors; pediatric; tuberous sclerosis complex.

Publication types

  • Case Reports
  • Research Support, Non-U.S. Gov't

MeSH terms

  • Child
  • Fibrous Dysplasia of Bone / complications*
  • Fibrous Dysplasia of Bone / diagnostic imaging
  • Humans
  • Infant
  • Magnetic Resonance Imaging
  • Male
  • Radiography
  • Ribs / abnormalities*
  • Ribs / diagnostic imaging
  • Spine / abnormalities*
  • Spine / diagnostic imaging
  • Tuberous Sclerosis / complications*
  • Tuberous Sclerosis / diagnostic imaging