[Splenomegaly and failure to thrive as a result of Gaucher disease]

Ugeskr Laeger. 2015 Sep 7;177(37):V04150358.
[Article in Danish]

Abstract

Gaucher disease (GD) is the most common lysosomal storage disease with a prevalence of 1:75,000. The disease is caused by a defiency of the lysosomal enzyme glucocerebrosidase which leads to an accumulation of the substrate glycosylceramide within macrophages. GD presents with a wide spectrum of symptoms but involvement of the bones, bone marrow and spleen or liver is seen in the majority of patients. We present the case of a ten-year-old girl with massive splenomegaly, cytopenia, poor growth, learning difficulties and extreme fatigue for several years.

Publication types

  • Case Reports

MeSH terms

  • Child
  • Failure to Thrive / etiology*
  • Female
  • Gaucher Disease / complications*
  • Humans
  • Somalia / ethnology
  • Splenomegaly / etiology*