Target engagement and drug residence time can be observed in living cells with BRET

Nat Commun. 2015 Dec 3:6:10091. doi: 10.1038/ncomms10091.

Abstract

The therapeutic action of drugs is predicated on their physical engagement with cellular targets. Here we describe a broadly applicable method using bioluminescence resonance energy transfer (BRET) to reveal the binding characteristics of a drug with selected targets within intact cells. Cell-permeable fluorescent tracers are used in a competitive binding format to quantify drug engagement with the target proteins fused to Nanoluc luciferase. The approach enabled us to profile isozyme-specific engagement and binding kinetics for a panel of histone deacetylase (HDAC) inhibitors. Our analysis was directed particularly to the clinically approved prodrug FK228 (Istodax/Romidepsin) because of its unique and largely unexplained mechanism of sustained intracellular action. Analysis of the binding kinetics by BRET revealed remarkably long intracellular residence times for FK228 at HDAC1, explaining the protracted intracellular behaviour of this prodrug. Our results demonstrate a novel application of BRET for assessing target engagement within the complex milieu of the intracellular environment.

Publication types

  • Evaluation Study

MeSH terms

  • Cell Proliferation
  • Cells / chemistry
  • Cells / cytology
  • Cells / drug effects*
  • Fluorescence Resonance Energy Transfer / methods*
  • HeLa Cells
  • Histone Deacetylase 1 / chemistry
  • Histone Deacetylase 1 / metabolism
  • Histone Deacetylase Inhibitors / chemistry*
  • Histone Deacetylase Inhibitors / pharmacology
  • Humans
  • Luciferases / chemistry
  • Luciferases / genetics
  • Luciferases / metabolism
  • Luminescence
  • Pharmaceutical Preparations / chemistry*

Substances

  • Histone Deacetylase Inhibitors
  • Pharmaceutical Preparations
  • Luciferases
  • Histone Deacetylase 1