Fully human MAP-fusion protein selectively targets and eliminates proliferating CD64(+) M1 macrophages

Immunol Cell Biol. 2016 May;94(5):470-8. doi: 10.1038/icb.2016.4. Epub 2016 Jan 8.

Abstract

Classical immunotoxins compromise a binding component (for example, a ligand, antibody or fragment thereof) and a cytotoxic component, usually derived from bacteria or plants (for example, Pseudomonas exotoxin A or ricin). Despite successful testing in vitro, the clinical development of immunotoxins has been hampered by immunogenicity and unsatisfactory safety profiles. Therefore, research has focused on fully human pro-apoptotic components suitable for the development of cytolytic fusion proteins (CFP). We recently reported that human microtubule-associated protein tau (MAP) can induce apoptosis when delivered to rapidly proliferating cancer cells. Here, we describe a new fully human CFP called H22(scFv)-MAP, which specifically targets CD64(+) cells. We show that H22(scFv)-MAP can efficiently kill proliferating HL-60 pro-monocytic cells in vitro. In addition, the human CFP specifically eliminates polarized M1 macrophages in a transgenic mouse model of cutaneous chronic inflammation. Because M1 macrophages promote the pathogenesis of many chronic inflammatory diseases, targeting this cell population with H22(scFv)-MAP could help to treat diseases such as atopic dermatitis, rheumatoid arthritis and inflammatory bowel disease.

MeSH terms

  • Animals
  • Apoptosis / drug effects
  • Cell Line
  • Cell Polarity* / drug effects
  • Cell Proliferation / drug effects
  • Cells, Cultured
  • Chronic Disease
  • Humans
  • Inflammation / pathology
  • Interferon-gamma / pharmacology
  • Macrophages / cytology*
  • Macrophages / drug effects
  • Macrophages / metabolism*
  • Mice
  • Microtubules / drug effects
  • Microtubules / metabolism
  • Protein Binding / drug effects
  • Receptors, IgG / metabolism*
  • Recombinant Fusion Proteins / pharmacology*
  • Single-Chain Antibodies / metabolism
  • Skin / pathology
  • tau Proteins / pharmacology*

Substances

  • MAPT protein, human
  • Receptors, IgG
  • Recombinant Fusion Proteins
  • Single-Chain Antibodies
  • tau Proteins
  • Interferon-gamma