Pharmacological Regulation of In Situ Tissue Stem Cells Differentiation for Soft Tissue Calcification Treatment

Stem Cells. 2016 Apr;34(4):1083-96. doi: 10.1002/stem.2306.

Abstract

Calcification of soft tissues, such as heart valves and tendons, is a common clinical problem with limited therapeutics. Tissue specific stem/progenitor cells proliferate to repopulate injured tissues. But some of them become divergent to the direction of ossification in the local pathological microenvironment, thereby representing a cellular target for pharmacological approach. We observed that HIF-2alpha (encoded by EPAS1 inclined form) signaling is markedly activated within stem/progenitor cells recruited at calcified sites of diseased human tendons and heart valves. Proinflammatory microenvironment, rather than hypoxia, is correlated with HIF-2alpha activation and promoted osteochondrogenic differentiation of tendon stem/progenitor cells (TSPCs). Abnormal upregulation of HIF-2alpha served as a key switch to direct TSPCs differentiation into osteochondral-lineage rather than teno-lineage. Notably, Scleraxis (Scx), an essential tendon specific transcription factor, was suppressed on constitutive activation of HIF-2alpha and mediated the effect of HIF-2alpha on TSPCs fate decision. Moreover, pharmacological inhibition of HIF-2alpha with digoxin, which is a widely utilized drug, can efficiently inhibit calcification and enhance tenogenesis in vitro and in the Achilles's tendinopathy model. Taken together, these findings reveal the significant role of the tissue stem/progenitor cells fate decision and suggest that pharmacological regulation of HIF-2alpha function is a promising approach for soft tissue calcification treatment.

Keywords: Calcification; Digoxin; HIF-2 alpha; Heart valves; Stem cells; Tendons.

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • Achilles Tendon / drug effects*
  • Achilles Tendon / growth & development
  • Achilles Tendon / pathology
  • Aged
  • Animals
  • Basic Helix-Loop-Helix Transcription Factors / antagonists & inhibitors
  • Basic Helix-Loop-Helix Transcription Factors / biosynthesis*
  • Basic Helix-Loop-Helix Transcription Factors / genetics
  • Calcinosis / drug therapy*
  • Calcinosis / genetics
  • Calcinosis / pathology
  • Cell Differentiation / genetics
  • Cell Proliferation / drug effects
  • Cells, Cultured
  • Cellular Microenvironment / drug effects
  • Chondrogenesis / genetics
  • Digoxin / administration & dosage
  • Humans
  • Male
  • Middle Aged
  • Rats
  • Rheumatic Heart Disease / genetics
  • Rheumatic Heart Disease / pathology
  • Stem Cells / drug effects
  • Stem Cells / pathology
  • Therapy, Soft Tissue*

Substances

  • Basic Helix-Loop-Helix Transcription Factors
  • SCX protein, human
  • endothelial PAS domain-containing protein 1
  • Digoxin