A novel small-molecule inhibitor of influenza A virus acts by suppressing PA endonuclease activity of the viral polymerase

Sci Rep. 2016 Mar 9:6:22880. doi: 10.1038/srep22880.

Abstract

The RNA-dependent RNA polymerase of influenza A virus comprises conserved and independently-folded subdomains with defined functionalities. The N-terminal domain of the PA subunit (PA(N)) harbors the endonuclease function so that it can serve as a desired target for drug discovery. To identify a class of anti-influenza inhibitors that impedes PA(N) endonuclease activity, a screening approach that integrated the fluorescence resonance energy transfer based endonuclease inhibitory assay with the DNA gel-based endonuclease inhibitory assay was conducted, followed by the evaluation of antiviral efficacies and potential cytotoxicity of the primary hits in vitro and in vivo. A small-molecule compound ANA-0 was identified as a potent inhibitor against the replication of multiple subtypes of influenza A virus, including H1N1, H3N2, H5N1, H7N7, H7N9 and H9N2, in cell cultures. Combinational treatment of zanamivir and ANA-0 exerted synergistic anti-influenza effect in vitro. Intranasal administration of ANA-0 protected mice from lethal challenge and reduced lung viral loads in H1N1 virus infected BALB/c mice. In summary, ANA-0 shows potential to be developed to novel anti-influenza agents.

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • Administration, Intranasal
  • Animals
  • Antiviral Agents / administration & dosage
  • Antiviral Agents / isolation & purification
  • Antiviral Agents / pharmacology*
  • Drug Evaluation, Preclinical
  • Drug Synergism
  • Female
  • Influenza A virus / drug effects*
  • Influenza A virus / enzymology*
  • Influenza A virus / physiology
  • Lung / virology
  • Mice, Inbred BALB C
  • Orthomyxoviridae Infections / pathology
  • Orthomyxoviridae Infections / prevention & control
  • Orthomyxoviridae Infections / virology
  • RNA-Dependent RNA Polymerase / antagonists & inhibitors*
  • Survival Analysis
  • Treatment Outcome
  • Viral Load
  • Viral Proteins / antagonists & inhibitors*
  • Virus Replication / drug effects*

Substances

  • Antiviral Agents
  • PA protein, influenza viruses
  • Viral Proteins
  • RNA-Dependent RNA Polymerase