Initial dual oral combination therapy in pulmonary arterial hypertension

Eur Respir J. 2016 Jun;47(6):1727-36. doi: 10.1183/13993003.02043-2015. Epub 2016 Mar 17.

Abstract

Treatment for pulmonary arterial hypertension (PAH) has been underpinned by single-agent therapy to which concomitant drugs are added sequentially when pre-defined treatment goals are not met.This retrospective analysis of real-world clinical data in 97 patients with newly diagnosed PAH (86% in New York Heart Association functional class III-IV) explored initial dual oral combination treatment with bosentan plus sildenafil (n=61), bosentan plus tadalafil (n=17), ambrisentan plus tadalafil (n=11) or ambrisentan plus sildenafil (n=8).All regimens were associated with significant improvements in functional class, exercise capacity, dyspnoea and haemodynamic indices after 4 months of therapy. Over a median follow-up period of 30 months, 75 (82%) patients were still alive, 53 (71%) of whom received only dual oral combination therapy. Overall survival rates were 97%, 94% and 83% at 1, 2 and 3 years, respectively, and 96%, 94% and 84%, respectively, for the patients with idiopathic PAH, heritable PAH and anorexigen-induced PAH. Expected survival rates calculated from the French equation for the latter were 86%, 75% and 66% at 1, 2 and 3 years, respectively.Initial combination of oral PAH-targeted medications may offer clinical benefits, especially in PAH patients with severe haemodynamic impairment.

MeSH terms

  • Adult
  • Aged
  • Antihypertensive Agents / administration & dosage
  • Bosentan
  • Diethylpropion
  • Drug Therapy, Combination
  • Familial Primary Pulmonary Hypertension / drug therapy*
  • Familial Primary Pulmonary Hypertension / physiopathology*
  • Female
  • Follow-Up Studies
  • Hemodynamics
  • Humans
  • Hypertension, Pulmonary / drug therapy*
  • Hypertension, Pulmonary / genetics
  • Hypertension, Pulmonary / physiopathology*
  • Male
  • Middle Aged
  • Patient Safety
  • Phenylpropionates / administration & dosage
  • Pyridazines / administration & dosage
  • Retrospective Studies
  • Severity of Illness Index
  • Sildenafil Citrate / administration & dosage
  • Sulfonamides / administration & dosage
  • Tadalafil / administration & dosage
  • Time Factors
  • Treatment Outcome

Substances

  • Antihypertensive Agents
  • Phenylpropionates
  • Pyridazines
  • Sulfonamides
  • Tadalafil
  • Sildenafil Citrate
  • ambrisentan
  • Bosentan
  • Diethylpropion