Transformative therapy in hypophosphatasia

Arch Dis Child. 2016 Jun;101(6):514-515. doi: 10.1136/archdischild-2015-309579. Epub 2016 Mar 18.
No abstract available

Keywords: Bone Disease; Bone Metabolism; Metabolic; Musculo-Skeletal; Therapeutics.

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • Alkaline Phosphatase / administration & dosage
  • Alkaline Phosphatase / blood
  • Alkaline Phosphatase / therapeutic use
  • Biomarkers / blood
  • Child
  • Child, Preschool
  • Enzyme Replacement Therapy / methods*
  • Humans
  • Hypophosphatasia / complications
  • Hypophosphatasia / diagnosis
  • Hypophosphatasia / drug therapy*
  • Immunoglobulin G / administration & dosage
  • Immunoglobulin G / therapeutic use
  • Infant
  • Infant, Newborn
  • Injections, Subcutaneous
  • Recombinant Fusion Proteins / administration & dosage
  • Recombinant Fusion Proteins / therapeutic use

Substances

  • Biomarkers
  • Immunoglobulin G
  • Recombinant Fusion Proteins
  • Alkaline Phosphatase
  • asfotase alfa