A translocator protein 18 kDa ligand, Ro5-4864, inhibits ATP-induced NLRP3 inflammasome activation

Biochem Biophys Res Commun. 2016 Jun 3;474(3):587-593. doi: 10.1016/j.bbrc.2016.04.080. Epub 2016 Apr 19.

Abstract

Ro5-4864 and PK11195, prototypical synthetic ligands of translocator protein 18 kDa (TSPO), have shown anti-inflammatory effects in several models of inflammatory diseases; however, their biochemical mechanisms remain poorly understood. Nod-like receptor family, pyrin domain containing 3 (NLRP3) inflammasome activation as a part of the innate immune system, has been implicated in a variety of inflammatory diseases. Here, we demonstrate for the first time that TSPO ligands, especially Ro5-4864, potently suppressed ATP-induced NLRP3 inflammasome activation in THP-1 and BMDM cells. Detailed action mechanism was further investigated in THP-1 cells. Ro5-4864 efficiently attenuated NLRP3 translocation to mitochondria, inflammasome assembly/oligomerization, activation of caspase-1, and subsequent secretion of the mature forms of interleukin-1β and -18. Ro5-4864 also reduced the production of mitochondrial superoxide and preserved the mitochondrial membrane potential in ATP-treated cells, suggesting that Ro5-4864 may act on mitochondria or more upstream targets in NLRP3 inflammasome signaling. We also observed the distinct effects of the TSPO ligands between THP-1 monocytes and macrophages, which suggested different NLRP3 inflammasome signaling depending on cell type. Collectively, our novel findings demonstrate that Ro5-4864 effectively inhibited ATP-induced NLRP3 inflammasome activation through the prevention of mitochondrial perturbation. Our results indicate Ro5-4864 as a promising candidate for the treatment of NLRP3 inflammasome-related diseases.

Keywords: Inflammasome; Mitochondria; NLRP3; Ro5-4864; TSPO.

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • Adenosine Triphosphate / immunology*
  • Benzodiazepinones / administration & dosage*
  • Cells, Cultured
  • Humans
  • Inflammasomes / drug effects
  • Inflammasomes / immunology*
  • Macrophage Activation / drug effects
  • Macrophage Activation / immunology*
  • Mitochondria / drug effects
  • Mitochondria / immunology
  • NLR Family, Pyrin Domain-Containing 3 Protein / immunology*
  • Protein Transport / drug effects
  • Protein Transport / immunology
  • Receptors, GABA / immunology*

Substances

  • Benzodiazepinones
  • Inflammasomes
  • NLR Family, Pyrin Domain-Containing 3 Protein
  • NLRP3 protein, human
  • Receptors, GABA
  • TSPO protein, human
  • 4'-chlorodiazepam
  • Adenosine Triphosphate