CD62L+ NKT cells have prolonged persistence and antitumor activity in vivo

J Clin Invest. 2016 Jun 1;126(6):2341-55. doi: 10.1172/JCI83476. Epub 2016 May 16.

Abstract

Vα24-invariant natural killer T cells (NKTs) localize to tumors and have inherent antitumor properties, making them attractive chimeric antigen receptor (CAR) carriers for redirected cancer immunotherapy. However, clinical application of CAR-NKTs has been impeded, as mechanisms responsible for NKT expansion and the in vivo persistence of these cells are unknown. Here, we demonstrated that antigen-induced expansion of primary NKTs in vitro associates with the accumulation of a CD62L+ subset and exhaustion of CD62L- cells. Only CD62L+ NKTs survived and proliferated in response to secondary stimulation. When transferred to immune-deficient NSG mice, CD62L+ NKTs persisted 5 times longer than CD62L- NKTs. Moreover, CD62L+ cells transduced with a CD19-specific CAR achieved sustained tumor regression in a B cell lymphoma model. Proliferating CD62L+ cells downregulated or maintained CD62L expression when activated via T cell receptor alone or in combination with costimulatory receptors. We generated HLAnull K562 cell clones that were engineered to express CD1d and costimulatory ligands. Clone B-8-2 (HLAnullCD1dmedCD86high4-1BBLmedOX40Lhigh) induced the highest rates of NKT expansion and CD62L expression. B-8-2-expanded CAR-NKTs exhibited prolonged in vivo persistence and superior therapeutic activities in models of lymphoma and neuroblastoma. Therefore, we have identified CD62L as a marker of a distinct NKT subset endowed with high proliferative potential and have developed artificial antigen-presenting cells that generate CD62L-enriched NKTs for effective cancer immunotherapy.

Publication types

  • Research Support, Non-U.S. Gov't
  • Research Support, N.I.H., Extramural

MeSH terms

  • Animals
  • Antigen-Presenting Cells / immunology
  • Cell Line, Tumor
  • Cell Proliferation
  • Cell Survival
  • Cells, Cultured
  • Cytokines / biosynthesis
  • Cytotoxicity, Immunologic
  • Humans
  • Immunotherapy, Adoptive
  • L-Selectin / metabolism*
  • Lymphocyte Activation
  • Lymphoma, B-Cell / immunology
  • Lymphoma, B-Cell / therapy
  • Mice
  • Mice, Inbred NOD
  • Mice, Knockout
  • Mice, SCID
  • Natural Killer T-Cells / classification
  • Natural Killer T-Cells / immunology*
  • Neuroblastoma / immunology
  • Neuroblastoma / therapy
  • Receptors, Antigen / immunology
  • Recombinant Fusion Proteins / immunology
  • Xenograft Model Antitumor Assays

Substances

  • Cytokines
  • Receptors, Antigen
  • Recombinant Fusion Proteins
  • SELL protein, human
  • L-Selectin