Mechanism, Consequences, and Therapeutic Targeting of Abnormal IL15 Signaling in Cutaneous T-cell Lymphoma

Cancer Discov. 2016 Sep;6(9):986-1005. doi: 10.1158/2159-8290.CD-15-1297. Epub 2016 Jul 15.

Abstract

Cutaneous T-cell lymphoma (CTCL) is the most common type of primary cutaneous lymphoma. Here, we report that patients with CTCL show increased IL15 in a clinical stage-dependent manner. Mechanistically, we show that ZEB1 is a transcriptional repressor of IL15 in T cells and that hypermethylation of the ZEB1 binding region within the IL15 promoter, as seen in patients with CTCL, prevents ZEB1 binding and causes increased transcription of IL15 Using a transgenic mouse model of IL15, we provide evidence that overexpression of IL15 induces a spontaneous CTCL that mimics the human neoplasm. Excessive autocrine production of IL15 in T cells inhibits an HDAC1-mediated negative autoregulatory loop, resulting in the upregulation of HDAC1 and HDAC6 and transcriptional induction of the onco-miR-21. Interruption of IL15 downstream signaling with isotype-specific HDAC inhibitors halts (HDAC1) or significantly delays (HDAC6) the progression of CTCL in vivo and provides preclinical evidence supporting a hierarchical model of oncogenic signaling in CTCL.

Significance: To date, CTCL pathogenesis remains unknown, and there are no curative therapies. Our findings not only demonstrate a critical role for IL15-mediated inflammation in cutaneous T-cell lymphomagenesis, but also uncover a new oncogenic regulatory loop in CTCL involving IL15, HDAC1, HDAC6, and miR-21 that shows differential sensitivity to isotype-specific HDAC inhibitors. Cancer Discov; 6(9); 986-1005. ©2016 AACR.This article is highlighted in the In This Issue feature, p. 932.

MeSH terms

  • Animals
  • Cell Line, Tumor
  • DNA Methylation / genetics
  • Gene Expression Regulation, Neoplastic
  • Histone Deacetylase 1 / biosynthesis
  • Histone Deacetylase 1 / genetics*
  • Histone Deacetylase 6
  • Histone Deacetylase Inhibitors / therapeutic use
  • Histone Deacetylases / biosynthesis
  • Histone Deacetylases / genetics*
  • Humans
  • Inflammation / genetics
  • Inflammation / pathology
  • Inflammation / therapy
  • Interleukin-15 / genetics*
  • Lymphoma, T-Cell, Cutaneous / genetics*
  • Lymphoma, T-Cell, Cutaneous / pathology
  • Lymphoma, T-Cell, Cutaneous / therapy
  • Mice
  • MicroRNAs / biosynthesis
  • MicroRNAs / genetics*
  • STAT3 Transcription Factor / genetics
  • Signal Transduction
  • Zinc Finger E-box-Binding Homeobox 1 / genetics

Substances

  • Histone Deacetylase Inhibitors
  • IL15 protein, human
  • Interleukin-15
  • MIRN21 microRNA, human
  • MicroRNAs
  • STAT3 Transcription Factor
  • STAT3 protein, human
  • ZEB1 protein, human
  • Zinc Finger E-box-Binding Homeobox 1
  • HDAC1 protein, human
  • HDAC6 protein, human
  • Histone Deacetylase 1
  • Histone Deacetylase 6
  • Histone Deacetylases